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Q.1
How many rare diseases have been identified?

Q.2
For people who have a rare disease, how many years, on average, did they wait to get an accurate diagnosis?

Q.3
How does the United States define a rare disease?

Q.4
How does the European Union define a rare disease?

Q.5
In the world, how many people have a rare disease?

Q.6
How many rare diseases have an approved treatment in the United States?

Q.7
How many treatments for rare diseases have been approved in the U.S. since 1983?

Q.8
A 2018 study counted the number of clinical trials in the U.S., Europe and Japan that investigated rare diseases and potential treatments. Out of 28,526 trials, how many were there?

Q.9
True or false: Newborn screening - testing babies at birth for certain conditions - is an important issue for rare disease advocates.

Q.10
When Is Rare Disease Day this year?

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